IPFに関わらず、様々な希少疾患についてまとめてみようと思います。何か創薬のヒントが見つかるかも知れません。 " Cerebral Adrenoleukodystrophy (cALD): Pathophysiology, Clinical Presentation, and Therapeutic Advances 1. Definition and EpidemiologyCerebral adrenoleukodystrophy (cALD) is the most severe phenotype of X-linked adrenoleukodystrophy (X-ALD), a …